Take a deep dive into one of the most awe-inspiring innovations of our time: gene therapy. This season, we’ll explore the infinite universe inside the tiny molecules of our DNA, and look at the technology with the potential to reshape our approach to treating many genetic diseases.
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Genetic screening is vital for early diagnosis and management of genetic diseases. Dig into how it works, how it can help treatments reach patients sooner, and how it informs traditional treatments like physical therapy.
Understand the different mechanisms by which gene therapy can potentially treat specific genetic diseases – such as amyotrophic lateral sclerosis, or ALS, and Duchenne muscular dystrophy, or DMD.
Adeno-associated viral vectors, or AAVs, are the tiny shells of viruses and are the most common vessels for delivering gene-based therapies. Launch into the past, present, and future of these viral rocket ships.
Peek into the future of gene therapy and its capacity to treat – maybe eliminate – genetic diseases like cancers and hemophilia. Plus, hear how gene therapy may be on the frontier of reversing the effects of aging.
While some genetic variations are positive, others can cause or contribute to disease. Learn how gene therapy replaces and repairs certain gene variants, and is changing the trajectory of genetic diseases.
Explore some of the major scientific findings – like discovering DNA – that set the stage for gene therapy, and its groundbreaking potential in the treatment of genetic diseases.
